🌍·Sep 9Industry
Efficacy results across a 12-month double-blind randomized trial and an open-label extension phase of arimoclomol for treatment of Niemann-Pick disease type C in patients treated with miglustat
Publisher
Z
Zevra Therapeutics
Global
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- Zevra Therapeutics
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- 最新
- Scope
- Industry
- Published
- September 9, 2025
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Source: Zevra Therapeutics
Scope: Industry
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