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🇬🇧·May 4Research

Clinical response to systemic AAV gene therapy in a large animal model of late-stage lysosomal storage disease

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N
Nature Gene Therapy

UK

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Publisher
Nature Gene Therapy
Region
UK
Scope
Research
Published
May 4, 2026

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Source: Nature Gene Therapy

Scope: Research

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Clinical response to systemic AAV gene therapy in a large animal model of late-stage lysosomal storage disease | Pharma Surge